Aartsma-Rus, A., Ferlini, A., Goemans, N., Pasmooij, A. M. G., Wells, D. J., Bushby, K., …Balabanov, P. Translational and Regulatory Challenges for Exon Skipping Therapies. HUMAN GENE THERAPY, 25(10), 885-892. https://doi.org/10.1089/hum.2014.086