TREATMENT WITH ORAL METFORMIN IMPROVES MUSCLE FUNCTION IN MDX MICE
Presentation / Conference Contribution
Terry, R. L., & Wells, D. J. TREATMENT WITH ORAL METFORMIN IMPROVES MUSCLE FUNCTION IN MDX MICE
Outputs (83)
POLOXOMER 188 HAS A DELETERIOUS EFFECT ON SKELETAL MUSCLE FUNCTION IN THE MDX MOUSE
Presentation / Conference Contribution
Terry, R. L., Kaneb, H. M., & Wells, D. J. POLOXOMER 188 HAS A DELETERIOUS EFFECT ON SKELETAL MUSCLE FUNCTION IN THE MDX MOUSE
OVER EXPRESSION OF THE LARGE TRANSGENE EXACERBATES MUSCLE PATHOLOGY IN THE MDX MOUSE
Presentation / Conference Contribution
Wells, K. E., Muses, S., Ruberg, A., Terry, R., Shihab, N. K., & Wells, D. J. OVER EXPRESSION OF THE LARGE TRANSGENE EXACERBATES MUSCLE PATHOLOGY IN THE MDX MOUSE
Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-esclation study
Journal Article
Cirak, S., Arechavala-Gomeza, V., Guglieri, M., Feng, L., Torelli, S., Anthony, K., Abbs, S., Garralda, M. E., Wells, D., Dickson, G., Wood, M. J. A., Wilton, S. D., Straub, V., Shrewsbury, S., Sewry, C., Morgan, J. E., Bushby, K., & Muntoni, F. Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-esclation study. https://doi.org/10.1016/S0140-6736%2811%2960756-3
RESTORING THE READING FRAME IN LARGE DMD DUPLICATION MUTATIONS RESULTS IN DYSTROPHIN EXPRESSION IN VIVO
Presentation / Conference Contribution
Muses, S., Jones, H., & Wells, D. J. RESTORING THE READING FRAME IN LARGE DMD DUPLICATION MUTATIONS RESULTS IN DYSTROPHIN EXPRESSION IN VIVO
INVESTIGATING THE EFFECTS OF DAO TRANSGENES ON THE SOD1(G93A) MOUSE MODEL OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
Presentation / Conference Contribution
Rahmani-Kondori, N., de Belleroche, J., & Wells, D. J. INVESTIGATING THE EFFECTS OF DAO TRANSGENES ON THE SOD1(G93A) MOUSE MODEL OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
Chronic Systemic Therapy With Low-dose Morpholino Oligomers Ameliorates the Pathology and Normalizes Locomotor Behavior in mdx Mice
Journal Article
Malerba, A., Graham, I., Sharp, P., Popplewell, L., Foster, K., Wells, D. J., & Dickson, G. Chronic Systemic Therapy With Low-dose Morpholino Oligomers Ameliorates the Pathology and Normalizes Locomotor Behavior in mdx Mice. Molecular Therapy, 19(2), 345-54. https://doi.org/10.1038/mt.2010.261
In vivo fluorescence lifetime tomography of a FRET probe expressed in mouse
Journal Article
McGinty, J., Stuckey, D. W., Solovjev, V. Y., Wylezinska-Arridge, M., Wells, D. J., Arridge, S. R., P M W, F., Hajnal, J. V., & Sardini, A. In vivo fluorescence lifetime tomography of a FRET probe expressed in mouse. Biomedical Optics Express, 2(7), 1907-1917. https://doi.org/10.1364/BOE.2.001907
Muscular dystrophies due to glycosylation defects: diagnosis and therapeutic strategies
Journal Article
Muntoni, F., Torelli, S., Wells, D. J., & Brown, S. C. Muscular dystrophies due to glycosylation defects: diagnosis and therapeutic strategies. Current Opinion in Neurology, 24(5), 437-442. https://doi.org/10.1097/WCO.0b013e32834a95e3
ARE LARGE-IN-FRAME DUPLICATIONS OF DYSTROPHIN FUNCTIONAL?
Presentation / Conference Contribution
Muses, S., Jones, H., & Wells, D. J. ARE LARGE-IN-FRAME DUPLICATIONS OF DYSTROPHIN FUNCTIONAL?