A Aartsma-Rus
Translational and Regulatory Challenges for Exon Skipping Therapies
Aartsma-Rus, A; Ferlini, A; Goemans, N; Pasmooij, A M G; Wells, D J; Bushby, K; Vroom, E; Balabanov, P
Authors
A Ferlini
N Goemans
A M G Pasmooij
D J Wells
K Bushby
E Vroom
P Balabanov
Citation
Aartsma-Rus, A., Ferlini, A., Goemans, N., Pasmooij, A. M. G., Wells, D. J., Bushby, K., …Balabanov, P. Translational and Regulatory Challenges for Exon Skipping Therapies. Human Gene Therapy, 25(10), 885-892. https://doi.org/10.1089/hum.2014.086
| Journal Article Type | Article |
|---|---|
| Deposit Date | Nov 11, 2014 |
| Publicly Available Date | Nov 21, 2020 |
| Journal | HUMAN GENE THERAPY |
| Print ISSN | 1043-0342 |
| Publisher | Mary Ann Liebert |
| Volume | 25 |
| Issue | 10 |
| Pages | 885-892 |
| DOI | https://doi.org/10.1089/hum.2014.086 |
| Public URL | https://rvc-repository.worktribe.com/output/1406260 |
| Additional Information | Corporate Creators : Duchenne Parent Project, European Med Agency, Ferrara, Italy, Groningen, Katholieke Univ Leuven, Leiden Uni Medical Center, Newcastle |
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