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All Outputs (358)

THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT
Presentation / Conference Contribution
Wells, D. J., Heslop, E., Csimma, C., Straub, V., McCall, J., Nagaraju, K., Wagner, K., Caizergues, D., Korinthenberg, R., Flanigan, K., Mendell, J., Kelly, M., Kaufmann, P., McNeil, E., Robertson, A., Johnston, L., & Bushby, K. THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT

FAT-HIPPO SIGNALLING IN BONE DEVELOPMENT
Presentation / Conference Contribution
Yiu, C. T., Zakaria, S., Shah, M., Mao, Y., Martin, T., Pitsillides, A. A., Irvine, K. D., & Francis-West, P. FAT-HIPPO SIGNALLING IN BONE DEVELOPMENT