E Heslop
The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development
Heslop, E; Csimma, C; Straub, V; McCall, J; Nagaraju, K; Wagner, K R; Caizergues, D; Korinthenberg, R; Flanigan, K M; Kaufmann, P; McNeil, E; Mendell, J; Hesterlee, S; Wells, D J
Authors
C Csimma
V Straub
J McCall
K Nagaraju
K R Wagner
D Caizergues
R Korinthenberg
K M Flanigan
P Kaufmann
E McNeil
J Mendell
S Hesterlee
D J Wells
Citation
Heslop, E., Csimma, C., Straub, V., McCall, J., Nagaraju, K., Wagner, K. R., …Wells, D. J. (in press). The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development. Orphanet Journal of Rare Diseases, 10(49), https://doi.org/10.1186/s13023-015-0258-1
Journal Article Type | Article |
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Acceptance Date | Mar 25, 2015 |
Deposit Date | May 22, 2015 |
Publicly Available Date | Nov 21, 2020 |
Journal | ORPHANET JOURNAL OF RARE DISEASES |
Publisher | BioMed Central |
Peer Reviewed | Peer Reviewed |
Volume | 10 |
Issue | 49 |
DOI | https://doi.org/10.1186/s13023-015-0258-1 |
Public URL | https://rvc-repository.worktribe.com/output/1401492 |
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