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THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT

Wells, D J; Heslop, E; Csimma, C; Straub, V; McCall, J; Nagaraju, K; Wagner, K; Caizergues, D; Korinthenberg, R; Flanigan, K; Mendell, J; Kelly, M; Kaufmann, P; McNeil, E; Robertson, A; Johnston, L; Bushby, K

Authors

D J Wells

E Heslop

C Csimma

V Straub

J McCall

K Nagaraju

K Wagner

D Caizergues

R Korinthenberg

K Flanigan

J Mendell

M Kelly

P Kaufmann

E McNeil

A Robertson

L Johnston

K Bushby



Citation

Wells, D. J., Heslop, E., Csimma, C., Straub, V., McCall, J., Nagaraju, K., Wagner, K., Caizergues, D., Korinthenberg, R., Flanigan, K., Mendell, J., Kelly, M., Kaufmann, P., McNeil, E., Robertson, A., Johnston, L., & Bushby, K. THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT

Presentation Conference Type Conference Abstract
Deposit Date Dec 17, 2015
Journal Neuromuscular Disorders
Print ISSN 0960-8966
Electronic ISSN 1873-2364
Publisher Elsevier
Volume 25
Pages S271-S271
DOI https://doi.org/10.1016/j.nmd.2015.06.308
Public URL https://rvc-repository.worktribe.com/output/1404473