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THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT

Wells, D J; Heslop, E; Csimma, C; Straub, V; McCall, J; Nagaraju, K; Wagner, K; Caizergues, D; Korinthenberg, R; Flanigan, K; Mendell, J; Kelly, M; Kaufmann, P; McNeil, E; Robertson, A; Johnston, L; Bushby, K

Authors

D J Wells

E Heslop

C Csimma

V Straub

J McCall

K Nagaraju

K Wagner

D Caizergues

R Korinthenberg

K Flanigan

J Mendell

M Kelly

P Kaufmann

E McNeil

A Robertson

L Johnston

K Bushby



Citation

Wells, D. J., Heslop, E., Csimma, C., Straub, V., McCall, J., Nagaraju, K., …Bushby, K. THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT. Neuromuscular Disorders, 25, S271-S271. https://doi.org/10.1016/j.nmd.2015.06.308

Journal Article Type Meeting Abstract
Deposit Date Dec 17, 2015
Journal Neuromuscular Disorders
Print ISSN 0960-8966
Publisher Elsevier
Volume 25
Pages S271-S271
DOI https://doi.org/10.1016/j.nmd.2015.06.308
Public URL https://rvc-repository.worktribe.com/output/1404473