D J Wells
THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT
Wells, D J; Heslop, E; Csimma, C; Straub, V; McCall, J; Nagaraju, K; Wagner, K; Caizergues, D; Korinthenberg, R; Flanigan, K; Mendell, J; Kelly, M; Kaufmann, P; McNeil, E; Robertson, A; Johnston, L; Bushby, K
Authors
E Heslop
C Csimma
V Straub
J McCall
K Nagaraju
K Wagner
D Caizergues
R Korinthenberg
K Flanigan
J Mendell
M Kelly
P Kaufmann
E McNeil
A Robertson
L Johnston
K Bushby
Citation
Wells, D. J., Heslop, E., Csimma, C., Straub, V., McCall, J., Nagaraju, K., …Bushby, K. THE TREAT-NMD ADVISORY COMMITTEE FOR THERAPEUTICS (TACT): AN INNOVATIVE DE-RISKING MODEL TO FOSTER ORPHAN DRUG DEVELOPMENT. Neuromuscular Disorders, 25, S271-S271. https://doi.org/10.1016/j.nmd.2015.06.308
Journal Article Type | Meeting Abstract |
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Deposit Date | Dec 17, 2015 |
Journal | Neuromuscular Disorders |
Print ISSN | 0960-8966 |
Publisher | Elsevier |
Volume | 25 |
Pages | S271-S271 |
DOI | https://doi.org/10.1016/j.nmd.2015.06.308 |
Public URL | https://rvc-repository.worktribe.com/output/1404473 |