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EXON SKIPPING AND DYSTROPHIN RESTORATION IN DUCHENNE MUSCULAR DYSTROPHY PATIENTS AFTER SYSTEMIC PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER TREATMENT

Cirak, S; Arechavala-Gomeza, V; Guglieri, M; Feng, L; Torelli, S; Anthony, K; Garralda, M E; Wells, D J; Dickson, G; Wood, M J A; Wilton, S D; Straub, V; Shrewsbury, S B; Sewry, C; Morgan, J E; Bushby, K; Muntoni, F

Authors

S Cirak

V Arechavala-Gomeza

M Guglieri

L Feng

S Torelli

K Anthony

M E Garralda

D J Wells

G Dickson

M J A Wood

S D Wilton

V Straub

S B Shrewsbury

C Sewry

J E Morgan

K Bushby

F Muntoni



Citation

Cirak, S., Arechavala-Gomeza, V., Guglieri, M., Feng, L., Torelli, S., Anthony, K., …Muntoni, F. EXON SKIPPING AND DYSTROPHIN RESTORATION IN DUCHENNE MUSCULAR DYSTROPHY PATIENTS AFTER SYSTEMIC PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER TREATMENT. Neuromuscular Disorders, 21(1), S7-S8

Journal Article Type Meeting Abstract
Deposit Date Nov 11, 2014
Journal Neuromuscular Disorders
Print ISSN 0960-8966
Publisher Elsevier
Volume 21
Issue 1
Pages S7-S8
Public URL https://rvc-repository.worktribe.com/output/1417768
Additional Information Corporate Creators : Acad Unit Child & Adol Pschy, AVI BioPharma, Guy's Hospital, London, Newcastle, Newcastle Uni, Australia, Oxford, Robert Jones & Agnes Hunt NHS Trust, Royal Holloway, Western Australia