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EXON SKIPPING AND DYSTROPHIN RESTORATION IN DUCHENNE MUSCULAR DYSTROPHY PATIENTS AFTER SYSTEMIC PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER TREATMENT

Cirak, S; Arechavala-Gomeza, V; Guglieri, M; Feng, L; Torelli, S; Anthony, K; Garralda, M E; Wells, D J; Dickson, G; Wood, M J A; Wilton, S D; Straub, V; Shrewsbury, S B; Sewry, C; Morgan, J E; Bushby, K; Muntoni, F

Authors

S Cirak

V Arechavala-Gomeza

M Guglieri

L Feng

S Torelli

K Anthony

M E Garralda

D J Wells

G Dickson

M J A Wood

S D Wilton

V Straub

S B Shrewsbury

C Sewry

J E Morgan

K Bushby

F Muntoni



Citation

Cirak, S., Arechavala-Gomeza, V., Guglieri, M., Feng, L., Torelli, S., Anthony, K., Garralda, M. E., Wells, D. J., Dickson, G., Wood, M. J. A., Wilton, S. D., Straub, V., Shrewsbury, S. B., Sewry, C., Morgan, J. E., Bushby, K., & Muntoni, F. EXON SKIPPING AND DYSTROPHIN RESTORATION IN DUCHENNE MUSCULAR DYSTROPHY PATIENTS AFTER SYSTEMIC PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER TREATMENT

Presentation Conference Type Conference Abstract
Deposit Date Nov 11, 2014
Journal Neuromuscular Disorders
Print ISSN 0960-8966
Electronic ISSN 1873-2364
Publisher Elsevier
Volume 21
Issue 1
Pages S7-S8
Public URL https://rvc-repository.worktribe.com/output/1417768
Additional Information Corporate Creators : Acad Unit Child & Adol Pschy, AVI BioPharma, Guy's Hospital, London, Newcastle, Newcastle Uni, Australia, Oxford, Robert Jones & Agnes Hunt NHS Trust, Royal Holloway, Western Australia




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